circRNA basic information
circBase ID: -
Name: hsa_circ_ARHGAP10
Synonym: circARHGAP10 / cARHGAP10
Host Gene: ARHGAP10
Genomic location(hg19): -
Genomic location(hg38): -
Subcellular localization: cytoplasm
 
 
 
 
 
 
 
Disease basic information
MONDO ID:
0008056
MONDO name: myotonic dystrophy type 1
Disease details: myotonic dystrophy type 1 / DM1
Disease DO ID:
11722
Disease MeSH ID:
-
Disease NCIt ID:
C84679
Disease ICD11 ID:
557405480
Disease OMIM ID:
160900
Species: Human
Species details: Homo sapiens
Tissue specimen:

biceps brachii muscle biopsies; tibialis anterior muscles; quadriceps muscles

Cell lines:

DM1-myogenic cells

In vivo animal model:

-

circRNA-disease information
Expression pattern:
UP
Associated gene: DMPK, AGO2
Associated microRNA: miR-409-3p
Biological function: Regulates DM1-associated molecular features; silencing reduces DMPK expression, decreases nuclear foci, and partially rescues splicing defects.
Molecular mechanism: Physical and functional interaction with miR-409-3p (co-regulation; RISC-associated); miR-409-3p overexpression counteracts effects of circARHGAP10 silencing.
Biological pathway or process:

ceRNA regulation (other); other pathway/process (other)

Detected method:
Q
S
Validation methods:

RNA-seq; RT-qPCR; RNase R Treatment; Sanger Sequencing; Back-Splice Junction PCR / divergent primers PCR; Nuclear-Cytoplasmic Fractionation; Clinical Sample Validation; Bioinformatics Analysis; Transfection; RNA Pull-Down; RIP (RNA Immunoprecipitation); FISH / smFISH; IF (Immunofluorescence); Western Blot; Annexin V/PI Flow Cytometry; ROC Analysis

Clinical significance:

Correlates positively with CTG repeat length and inversely with muscle strength; circ/lin ratio shows diagnostic potential (ROC AUC 0.86) to discriminate DM1 patients from controls.

Description:

circARHGAP10 is upregulated in DM1 skeletal muscle and shows biomarker potential (correlates with CTG repeat length and muscle strength; ROC AUC 0.86). Functionally, circARHGAP10 knockdown in DM1 myogenic cells reduces DMPK levels, decreases toxic nuclear RNA foci, and partially rescues missplicing, with effects mediated at least partly through interaction/co-regulation with miR-409-3p.

Confidence score:

0.8635

Other information
Title:

circARHGAP10 as a candidate biomarker and therapeutic target in myotonic dystrophy type 1.

Journal: Molecular therapy. Nucleic acids
Published: 2025
PubMed ID: 40896579
Study type:

combined biological and clinical study

Data availability: GSE86356; GSE201255; GSE111016; GSE111010; GSE202745; Supplemental information (https://doi.org/10.1016/j.omtn.2025.102646)
Code availability: -